Research

Finding unique research projects is at the heart of what we do.

Research

Great Ormond Street Hospital Children's Charity Base Editing Repair for Gentle Repair of Fragile DNA Disorders

In January 2024, we announced our collaboration with Great Ormond Street Hospital Children's Charity (GOSH Charity), where Noah was treated and lost his fight on 05th June 2020. This research project led by Professor Waseem Qasim will investigate and progress a new DNA editing technique as a safer, more effective alternative to stem cell transplantation.

Stem cell transplants are often a vital part of blood cancer treatment, and this technique will also help children with genetic disorders.

We have a minimum funding target of £125,000 for this project.

Research

MRC Centre for Medical Mycology, University of Exeter Noah’s Pink Balloon Fellowship

Our first project was with the MRC Centre for Medical Mycology at the University of Exeter for research into the deadly fungal infection mucormycosis, a feared complication in patients undergoing chemotherapy for Leukaemia and other malignancies, and in patients receiving a bone marrow or solid organ transplant.

Thanks to your support, we donated £110,000 and Noah’s Fellow, Dr. Alyssa Hudson graduated in December 2023.